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尽管目前全球仅有5000名婴幼儿使用该药,但罕见病药物的高定价模式,叠加长期持续给药的治疗需求,让Vosoritide的商业表现持续走高。2025年,该药销售额达9.27亿美元,同比增长26%,是BioMarin的核心商业化增长引擎。
"Had I not have heard [the smoke alarm], I would have just been in there," says McConnell. "They are essential, absolutely essential.",详情可参考搜狗输入法下载
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